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Diseases
Treated
Allogeneic and autologous transplants are performed for
pediatric patients with the following diseases:
- Acute Leukemia
- Acute Lymphoblastic Leukemia (ALL) in remission
- Infant ALL (MLL or 11q23+)
- T-cell ALL
- B-precursor ALL
- Ph+ ALL (T 9;11)
- ALL with high risk features in first remission at diagnosis including
T4;11, MLL, T1;19, WBC>300K
- Acute Non-Lymphocytic Leukemia (ANLL)
- Acute Myelogenous Leukemia (AML)
- Secondary AML
- Acute Undifferentiated Leukemia
- Stem Cell Leukemia
- Biphenotypic Leukemia
- Chronic Leukemia
- Chronic Myelogenous Leukemia (CML)
- Juvenile CML (JCML) or CMML
- Myelodysplastic Syndromes (MDS)
- MDS
- Monosomy 7
- Monosomy 5
- Lymphoma
- Non-Hodgkin’s Lymphoma (NHL)
- Lymphoblastic Lymphoma
- Burkitt’s Lymphoma
- Large Cell Lymphoma
- Mantle Cell Lymphoma
- Histiocytic Lymphoma
- Hodgkin’s Disease (HD)
- Brain Tumors
- Medulloblastoma
- Astrocytoma
- Pineoblastoma
- Retinoblastoma
- Glioblastoma Multiforme
- PNET
- Rhabdoid Brain Tumors
- Solid Tumors
- Neuroblastoma
- Wilm’s Tumor
- Rhabdomyosarcoma
- Ewing’s Sarcoma
- Osteogenic Sarcoma
- Retinoblastoma
- PNET
- Immunodeficiency Syndromes
- Severe Combined Immunodeficiency Syndrome (SCID)
- X-Linked SCID
- ADA Deficiency
- PNP Deficiency
- Nezelof’s Syndrome
- Zap-70 Deficiency
- Idiopathic SCID
- CID
- X-Linked Lymphoproliferative Syndrome
- Common Variable Immunodeficiency Disease (CVID)
- Wiskott-Aldrich Syndrome (WAS)
- Cartiledge-Hair Hypoplasia
- Reticular Dysgenesis
- Familial Erythrophagocytic Lymphohistiocytosis (FEL)
- Histiocytic Syndromes
- White Blood Cell Disorders
- Leukocyte Adhesion Deficiency (LAD)
- (LFA-1 Deficiency, CD11/18)
- Chronic Granulomatous Disease (CGD)
- Chediak Higashi Syndrome
- Kostmann’s Syndrome (Congenital Neutropenia)
- Red Blood Cell Disorders
- Sickle Cell Anemia
- Thalassemia Major
- Blackfan-Diamond Anemia
- (Congenital Pure Red Cell Aplasia)
- Sideroblastic Anemia
- Other transfusion-dependent anemias
- Platelet Disorders
- Amegakaryocytic Thrombocytopenia (AMT)
- Thrombocytopenia with Absent Radii (TAR) Syndrome
- Bone Marrow Failure Disorders
- Fanconi Anemia
- Congenital Aplastic Anemia
- Dyskeratosis Congenita
- Acquired Severe Aplastic Anemia
- Paroxsysmal Nocturnal Hemoglobinuria (PNH)
- Amegakaryocytic Thrombocytopenia (AMT)
- Inborn Errors of Metabolism
- Mucopolysaccharidoses
- Hurler Syndrome (MPI)
- Hurler-Scheie
- San Filippo Syndrome
- Maroteaux-Lamy Syndrome (MP VI)
- Leukodystrophies
- Adrenoleukodystrophy (ALD)
- Krabbe Disease (Globoid Leukodystrophy)
- Metachromatic Leukodystrophy (MLD)
- Others
- Osteopetrosis
- Niemann-Pick Disease (Types A and B)
- Lesch-Nyhan Syndrome
- Hypophosphatasia
- Gaucher Disease
- Mannosidosis
- Tay Sachs Disease (GM2)
GM1
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